Systemic Administration of Tripeptidyl Peptidase I in a Mouse Model of Late Infantile Neuronal Ceroid Lipofuscinosis: Effect of Glycan Modification
journals.plos.org/plosone/article?id=10.1371/journal.pone.0040509
May 31, 2026
1
Restoration of progranulin by engineered hematopoietic stem cell–derived microglia corrects phenotypes of granulin knockout mice
www.science.org/doi/10.1126/scitranslmed.adw9930?url_ver=Z39.88-2003&rfr_id=ori:rid:crossref.org&rfr_dat=cr_pub%20%200pubmed
May 31, 2026
1
Enzyme replacement therapy for CLN1 batten disease that crosses the blood-brain-barrier
www.sciencedirect.com/science/article/abs/pii/S1096719226000168?via%3Dihub
May 31, 2026
32
Enhancing prenatal spinal surgery with stem cells
www.nature.com/articles/d41591-026-00017-3
Apr 9, 2026
1
Blood-brain barrier disruption, traumatic encephalopathy, and cognitive decline in retired athletes
www.science.org/doi/abs/10.1126/scitranslmed.adu6037?af=R
Apr 9, 2026
1
患者1人約3億円の遺伝子治療を「誰もが使える医療」へ、ノーベル賞科学者が挑むエコシステム構想 | Forbes JAPAN 公式サイト（フォーブス ジャパン）
forbesjapan.com/articles/detail/92463/page2
Mar 15, 2026
1
YouTubeで効率的に学ぶ方法：科学に基づく動画学習ガイド | Glasp
glasp.co/articles/how-to-learn-from-youtube/ja
Mar 15, 2026
4
スマートノートの取り方：注釈とナレッジ構築のガイド | Glasp
glasp.co/articles/how-to-take-smart-notes/ja
Mar 15, 2026
4
Just a moment...
www.biorxiv.org/content/10.64898/2026.02.23.707565v1
Mar 9, 2026
An innovative hematopoietic stem cell gene therapy approach benefits CLN1 disease in the mouse model - EMBO Molecular Medicine
link.springer.com/article/10.15252/emmm.202215968
Feb 28, 2026
2215
Cause for Progressive Blindness Identified
www.genengnews.com/topics/translational-medicine/cause-for-progressive-blindness-identified/
Feb 21, 2026
1
Oligodendrocyte Differentiation Holds Promise for MS Treatment Development
www.genengnews.com/topics/translational-medicine/oligodendrocyte-differentiation-holds-promise-for-ms-treatment-development/
Jan 30, 2026
11
Cell-type resolved protein atlas of brain lysosomes identifies SLC45A1-associated disease as a lysosomal disorder
www.cell.com/cell/fulltext/S0092-8674(25)01425-4?_returnURL=https%3A%2F%2Flinkinghub.elsevier.com%2Fretrieve%2Fpii%2FS0092867425014254%3Fshowall%3Dtrue
Jan 30, 2026
1
Cell-Type Atlas of Brain Lysosomal Proteins May Clarify Neurological Disorders
www.genengnews.com/topics/translational-medicine/cell-type-atlas-of-brain-lysosomal-proteins-may-clarify-neurological-disorders/
Jan 30, 2026
41
Lysosomal Brain Protein Atlas
brainresilience.stanford.edu/lysosomal-brain-protein-atlas
Jan 30, 2026
1
Treatment of Inherited Eye Defects by Systemic Hematopoietic Stem Cell Transplantation | IOVS | ARVO Journals
iovs.arvojournals.org/article.aspx?articleid=2469222
Jan 12, 2026
21
Frontiers | The Contribution of Microglia to the Development and Maturation of the Visual System
www.frontiersin.org/journals/cellular-neuroscience/articles/10.3389/fncel.2021.659843/full
Jan 12, 2026
99
(PDF) Roles of Drug Transporters in Blood-Retinal Barrier
www.researchgate.net/publication/336168617_Roles_of_Drug_Transporters_in_Blood-Retinal_Barrier/figures?lo=1&utm_medium=&utm_campaign=
Jan 12, 2026
1
網膜 - 脳科学辞典
bsd.neuroinf.jp/wiki/%E7%B6%B2%E8%86%9C
Jan 12, 2026
3
ミュラーグリア - 脳科学辞典
bsd.neuroinf.jp/wiki/%E3%83%9F%E3%83%A5%E3%83%A9%E3%83%BC%E3%82%B0%E3%83%AA%E3%82%A2
Jan 12, 2026
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視細胞 - 脳科学辞典
bsd.neuroinf.jp/wiki/%E8%A6%96%E7%B4%B0%E8%83%9E
Jan 12, 2026
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網膜色素変性の過蛍光リング – 目医者情報
meisha.info/archives/744
Jan 12, 2026
1
網膜色素変性 – 目医者情報
meisha.info/archives/726
Jan 12, 2026
11
CNS infection and immune privilege - Nature Reviews Neuroscience
www.nature.com/articles/s41583-018-0070-8
Jan 12, 2026
11
2025 FDA approvals
www.nature.com/articles/d41573-026-00001-z
Jan 7, 2026
1
BioMarin to buy Amicus Therapeutics for $4.8B, bringing together rare disease biotechs
www.statnews.com/2025/12/19/biomarin-amicus-acquisition-rare-disease-fabry-pompe/
Jan 5, 2026
1
An AAV variant selected through NHP screens robustly transduces the brain and drives secreted protein expression in NHPs and mice
www.science.org/doi/10.1126/scitranslmed.adr2531
Jan 5, 2026
22